Intrathecal 2-Hydroxypropyl-ß-cyclodextrin for neurological decline in patients with Niemann-Pick disease type C1,
Role: PI,
Rush University Medical Center,
(12/2024 - 12/2025)
Status: Approved
REACH: Randomised Trial of Rehabilitation Very Early in Congenital Hemiplegia
Site Principal Investigator
(01/2019 - 05/2020)
Pharmacokinetics of Botulism Antitoxin Heptavalent (A, B, C, D, E, F, G) – (Equine) (BATTM) in Pediatric Patients with a Confirmed or Suspected Exposure to Botulinum Toxin
Sub-investigator
(05/2017 - 12/2017)